Title:
CRISPR-CAS13 SYSTEM FOR TREATING SOD1-ASSOCIATED DISEASES
Document Type and Number:
WIPO Patent Application WO/2023/024504
Kind Code:
A1
Abstract:
The invention provides an CRISPR-Cas13 system and a method of treating SOD1-associated diseases with the same.
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Inventors:
YANG HUI (CN)
WANG XING (CN)
BAI MINGLIANG (CN)
WANG XING (CN)
BAI MINGLIANG (CN)
Application Number:
PCT/CN2022/083476
Publication Date:
March 02, 2023
Filing Date:
March 28, 2022
Export Citation:
Assignee:
HUIGENE THERAPEUTICS CO LTD (CN)
CENTER FOR EXCELLENCE IN BRAIN SCIENCE AND INTELLIGENCE TECH CHINESE ACADEMY OF SCIENCES (CN)
CENTER FOR EXCELLENCE IN BRAIN SCIENCE AND INTELLIGENCE TECH CHINESE ACADEMY OF SCIENCES (CN)
International Classes:
C12N9/78; A61K35/17; C12N9/22; C12N15/10; C12N15/82
Domestic Patent References:
WO2018002762A1 | 2018-01-04 |
Foreign References:
US20210093667A1 | 2021-04-01 | |||
CN111511388A | 2020-08-07 | |||
CN111727247A | 2020-09-29 | |||
CN111328290A | 2020-06-23 |
Other References:
M. ALEJANDRA ZEBALLOS ET AL.: "Next-Generation CRISPR Technologies and Their Applications in Gene and Cell Therapy", TRENDS IN BIOTECHNOLOGY, vol. 39, no. 7, 30 June 2021 (2021-06-30), XP086612147, ISSN: 0167-7799, DOI: 10.1016/j.tibtech.2020.10.010
Attorney, Agent or Firm:
SHANGHAI PATENT & TRADEMARK LAW OFFICE, LLC (CN)
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